Hypoxanthine-guanine phosphoribosyltransferase deficiency (HPRT-d): cascade genetic screening in an affected family with HPRT1 c.584A> C mutation

Abstract:  The hypoxanthine-guanine phosphoribosyltransferase deficiency (HPRT-d) is an inborn error in purine metabolism with X-linked inheritance responsible for Lesch-Nyhan disease (LND) and its attenuated variants (LNV). LND shows a totally enzymatic deficiency and it`s characteriz...

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Autores principales: Luna Pizarro , AG, Grosso , CL, Laróvere , LE
Formato: Artículo revista
Publicado: Universidad Nacional Córdoba. Facultad de Ciencias Médicas. Secretaria de Ciencia y Tecnología 2021
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Acceso en línea:https://revistas.unc.edu.ar/index.php/med/article/view/35076
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